A biopharmaceutical company advancing gene therapy platforms to help address unmet needs in neurodegenerative diseases.
GenSight is an innovative clinical-stage biopharmaceutical company. Our mission is to apply scientific and technological advances in gene therapy to help support an unmet need in people with severe degenerative diseases of the eye and central nervous system.
We are investigating a platform based on the combination of a gene therapy-based approach with technologies such as:
For an overview of these platforms, go to Our technologies.
Our team is driven by their experience, expertise and commitment to supporting people with rare diseases. Together, we have over 40 years of experience in the pharmaceutical sector.
For more information about the diseases we target, our technology platforms or our partnerships, please click below.